New platform aims to develop novel therapies for rare diseases

Updated: Feb 2 2023 1:25PM

New Delhi, Feb 2 (PTI) Researchers are working on a new platform that aims to develop several treatments, including gene and mRNA therapies, for three "rare" diseases which are estimated to affect about one million people in India.

The Myo-Mission anchored by Ashoka University, Sonipat in partnership with 18 institutions and 38 investigators across India, will enhance capabilities for carrying out future clinical trials for Duchene Muscular Dystrophy, GNE Myopathy and Limb-Girdle Muscular Dystrophy (LGMD).

All the three diseases either lead to muscular weakness or muscle wasting, and can cause permanent disability.